Clinical Studies and Trials

A-T Biomarker Development Initiative Now Recruiting

Dec 18, 2023 Comments Off on A-T Biomarker Development Initiative Now Recruiting
Mar 1 @ 12:54 pm

On December 18, the A-T Children’s Project sent out the below email to A-T parents in the United States inviting their children with and without A-T to participate in the A-T Biomarker Development Initiative. THE A-T BIOMARKER DEVELOPMENT INITIATIVE Join us in identifying desperately needed biomarkers to improve the development…

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Promising Study Finds Ways to Measure A-T

Apr 14, 2022 Comments Off on Promising Study Finds Ways to Measure A-T
Mar 1 @ 12:54 pm

Dear Friends, We are excited to share the following update from Dr. Anoopum Gupta to the A-T families who have been participating in his project to find better ways to measure A-T. We are so grateful to him, to the families, and, of course, to our donors and fundraisers who…

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Intrabio – Clinical Trial Expansion

Mar 1, 2021 Comments Off on Intrabio – Clinical Trial Expansion
Mar 1 @ 12:54 pm

On February 16, 2021, the A-T Children’s Project sent the below email to A-T families in the United States announcing that the pharmaceutical company IntraBio has expanded their clinical trial to test N-Acetyl-L-Leucine in A-T patients, and we will be helping with recruitment.  Dear A-T Parents, Last year, we let…

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A Biomarker to Track Brain Cell Death in A-T Kids

Jun 4, 2020 Comments Off on A Biomarker to Track Brain Cell Death in A-T Kids
Mar 1 @ 12:54 pm

Hi everyone, I hope you and your families are continuing to stay safe during the pandemic. Over the past year, you’ve heard me talk a lot about testing an approach called antisense oligonucleotide (ASO) gene therapy in a little girl with   A-T. She has continued to receive regular injections, and…

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A-T ASO Gene Therapy Trial Continues!

Apr 17, 2020 Comments Off on A-T ASO Gene Therapy Trial Continues!
Mar 1 @ 12:54 pm

Hi everyone, I hope you and your family are doing well and keeping safe. As much as the COVID-19 pandemic has changed our world, I wanted to let you know that our ASO gene therapy trial for A-T – that you helped make possible – has not stopped. It continues…

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