Research Updates

An ASO is Working in an A-T Child’s Cells!

Aug 31, 2018 Comments Off on An ASO is Working in an A-T Child’s Cells!
Jun 21 @ 1:16 am

Email from Volunteer Chairman and Founder, Brad Margus: As you know, to develop an urgently needed treatment for A-T, we’ve been eager to use a gene therapy approach called “antisense oligonucleotide” or “ASO” therapy to produce a functional ATM protein in children who have A-T. While (with your help!) we’ve…

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Making Brain Cells from A-T Patients

Aug 16, 2018 Comments Off on Making Brain Cells from A-T Patients
Jun 21 @ 1:16 am
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Identifying Factors That Impact Growth in A-T

Jul 18, 2018 Comments Off on Identifying Factors That Impact Growth in A-T
Jun 21 @ 1:16 am
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Sequencing RNA in Search of A-T Biomarkers

Jun 22, 2018 Comments Off on Sequencing RNA in Search of A-T Biomarkers
Jun 21 @ 1:16 am
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Imaging the Changing Cerebellum in A-T

Apr 11, 2018 Comments Off on Imaging the Changing Cerebellum in A-T
Jun 21 @ 1:16 am
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Timeline and Progress for Aso Gene Therapy

Apr 11, 2018 Comments Off on Timeline and Progress for Aso Gene Therapy
Jun 21 @ 1:16 am
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Making A-T Stem Cells Broadly Available

Dec 20, 2017 Comments Off on Making A-T Stem Cells Broadly Available
Jun 21 @ 1:16 am

 

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Reducing A-T Severity by Targeting Other Genes

Jul 30, 2017 Comments Off on Reducing A-T Severity by Targeting Other Genes
Jun 21 @ 1:16 am
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Applying Machine Learning to A-T

Jul 20, 2017 Comments Off on Applying Machine Learning to A-T
Jun 21 @ 1:16 am
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Targeting Neutrophil-driven Inflammation to Reduce Lung Problems in A-T

May 5, 2017 Comments Off on Targeting Neutrophil-driven Inflammation to Reduce Lung Problems in A-T
Jun 21 @ 1:16 am
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