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Gene Therapy for A-T

November 18 - 20, 2024

Boston, Massachusetts, USA

Dates: Monday, November 18 at 7 PM - Wednesday, November 20 at 5 PM

Location: Hyatt Regency Boston Harbor (at Boston Logan Airport), Boston, Massachusetts, USA

An in-person meeting where scientists and clinicians will:
  • Present their progress to date on efforts to treat ataxia-telangiectasia (A-T) using antisense oligonucleotides (ASOs)
  • Propose and evaluate other, emerging gene editing and replacement technologies that may be feasible for A-T
  • Assess biomarkers and innovative clinical trial designs
  • Share functional assays, tools, data and resources
  • Identify gaps where increased investment is needed
  • Form collaborations to plan next steps

Participation is limited to the scientific community and industry experts. Please complete the information below to register.

Due to the global tech outages today, July 19, you may have trouble registering on this page.

Please give us a call at 954-481-6611 and we will be happy to assist you in making your donation. Thank you for your patience and support!


Please email Jennifer Thornton, Executive Director at or call/text her directly at +1.561.306.2826.