Rare Disease Day Thursday, Feb 29, 2024

The nonprofit A-T Children’s Project partners with academic and industry investigators worldwide – organizing and supporting innovative research, conferences, clinical teams, data platforms and biomarker development – to optimize disease management strategies, develop new treatments and find a cure.

Because of contributions like yours, there are exciting A-T research advances happening on several fronts. These include pushing towards new ways to discover drugs; to advance gene therapy and editing approaches to treat A-T; and, to find robust ways to measure A-T to track disease progression and tell us more objectively, precisely and quickly if a clinical trial is working.